autonomic pharmacology · cholinergic system

Cholinergic Neuroeffector Pharmacology

Receptor activation, inhibition, and clinical integration — high‑yield for USMLE

Synthesis, storage, and release of ACh

  • Choline uptake: Na⁺‑dependent transporter (similar to SGLT)
  • Rate‑limiting step: choline acetyltransferase (ChAT)
  • Vesicular storage: protons exchanged for ACh (vesicular transporter)
  • Release: Ca²⁺‑dependent exocytosis at the neuroeffector junction
  • Termination: acetylcholinesterase (AChE) hydrolyzes ACh → choline + acetate
  • Choline reuptake: high‑affinity, recycled for new synthesis
⏳ Botulinum toxin: prevents vesicle docking & release (cleaves SNARE proteins)
🧪 Hemicholinium: blocks choline reuptake → depletes ACh
Choline ChAT ACh Vesicle exocytosis AChE choline

🔬 Cholinergic receptor families

  • Muscarinic (M1–M5) — GPCR, slow response
  • M1, M3, M5: Gq → PLC ↑ → IP₃ / DAG / Ca²⁺
  • M2, M4: Gi → adenylyl cyclase ↓ → cAMP ↓
  • Nicotinic (N) — ligand‑gated ion channel, fast response
  • NN: autonomic ganglia, adrenal medulla
  • NM: neuromuscular junction (skeletal muscle)
ReceptorCouplingEffector
M1, M3, M5Gq↑ PLC → IP₃, DAG, Ca²⁺
M2, M4Gi↓ adenylyl cyclase → ↓ cAMP
NN, NMion channelNa⁺/K⁺ flux → depolarisation
⚠️ N receptors desensitise rapidly with sustained agonist exposure

💊 Muscarinic receptor agonists

  • Bethanechol — M‑selective (no CNS)
  • Uses: postoperative ileus, neurogenic urinary retention
  • Methacholine — M > N, diagnostic for bronchial hyperreactivity
  • Pilocarpine / Cevimeline — M‑selective
  • Xerostomia (Sjögren, radiation), glaucoma (pilocarpine topical)
  • ACh — rapidly hydrolysed, no clinical use
📌 Pilocarpine: direct M agonist, lowers IOP by increasing aqueous outflow

🧪 Acetylcholinesterase inhibitors (indirect agonists)

  • Edrophonium — short acting, diagnostic for myasthenia gravis
  • Physostigmine — tertiary amine, enters CNS
  • Glaucoma, atropine overdose (antidote)
  • Neostigmine / Pyridostigmine — quaternary, no CNS
  • Ileus, urinary retention, myasthenia gravis, reverse NM blockade
  • Donepezil / Rivastigmine — lipid soluble, CNS, Alzheimer disease
  • Organophosphates — irreversible, lipid soluble
  • Insecticides (malathion, parathion), nerve agents (sarin)
DrugPropertiesKey use
Edrophoniumshort actingmyasthenia gravis diagnosis
Physostigminetertiary, CNSatropine OD, glaucoma
Neostigminequaternary, no CNSileus, reversal of NM block
Donepezillipophilic, CNSAlzheimer disease
⚠️ Organophosphate toxicity: muscarinic + nicotinic excess. Atropine for muscarinic effects; pralidoxime (2‑PAM) to reactivate AChE (must be given before aging).
  • Toxicity features: salivation, lacrimation, urination, diarrhoea, bradycardia, bronchoconstriction, muscle fasciculations → paralysis

🚫 Muscarinic receptor antagonists

  • Atropine — prototype, tertiary amine (CNS entry)
  • Effects (dose‑dependent): ↓ secretions, mydriasis, cycloplegia, tachycardia, hyperthermia, sedation, urinary retention
  • Antidote for AChE inhibitor poisoning (muscarinic effects)
  • Ipratropium / Tiotropium — inhalational, no CNS, asthma/COPD
  • Scopolamine — motion sickness, sedation, short‑term memory block
  • Oxybutynin — overactive bladder (urge incontinence)
  • Benzatropine / Trihexyphenidyl — lipid soluble, parkinsonism, EPS
🧠 Atropine overdose: “hot as a hare, blind as a bat, dry as a bone, red as a beet, mad as a hatter” — supportive + physostigmine if severe

Nicotinic receptor antagonists

  • Ganglion blockers — hexamethonium, mecamylamine
  • Block both SANS and PANS ganglia → loss of autonomic tone
  • Effects: vasodilation, hypotension, reflex tachycardia (blocked), constipation, urinary retention, anhidrosis
  • Neuromuscular blockers — see anaesthetics section
  • Non‑depolarising (e.g., rocuronium) vs depolarising (succinylcholine)
SystemEffect of ganglion blockade
Arteriolesvasodilation (↓ SANS tone)
Heart (SA node)tachycardia (loss of PANS tone)
GI tract↓ motility → constipation
Bladderurinary retention
Sweat glandsanhidrosis (loss of SANS)

🩺 Clinical pearls & high‑yield facts

  • Alzheimer disease: loss of cholinergic neurons in nucleus basalis of Meynert → AChE inhibitors (donepezil) provide modest symptomatic benefit
  • Atropine: order of effects — secretions ↓, mydriasis, tachycardia, hyperthermia, CNS excitation
  • Physostigmine crosses BBB; neostigmine does not — useful for central anticholinergic syndrome
  • Organophosphate poisoning: “SLUDGE” (salivation, lacrimation, urination, diarrhoea, GI upset, emesis) + muscle twitching
  • Pralidoxime (2‑PAM): reactivates AChE only before “aging” (covalent bond stabilises)
  • Dual innervation: PANS dominates heart (SA/AV), pupil, GI, bladder; SANS dominates vascular tone & sweat glands
📌 Exam trap: myasthenia gravis — edrophonium (short) improves; atropine is used for cholinergic crisis (overmedication with AChE inhibitors)