USMLE Step 1 · High-Yield

Pharmacology Revision Notes

Complete drug-class-by-drug-class review · 31 chapters · 11 units

Concise, exam-focused revision notes covering autonomic, cardiovascular, CNS, antimicrobial, endocrine, respiratory, GI, hematologic, and oncologic pharmacology — with tables, flowcharts, mnemonics, and clinical pearls.

USMLE Focused High-Yield Drug Classes Free Forever
⚖️

General Principles

2 topics

📘 Pharmacodynamics & Pharmacokinetics

  • Affinity – ability to bind receptor; inversely related to Kd
  • Potency – dose needed for 50% effect (EC50); leftward shift = more potent
  • Efficacy – maximal effect (ceiling); full agonists = 100%, partial agonists = lower
  • Competitive antagonist – shifts curve rightward (parallel), overcome by ↑ agonist
  • Non-competitive antagonist – reduces efficacy (lower ceiling)
G-proteinEffectorSecond MessengerExample Receptors
Gs↑ Adenylyl cyclase↑ cAMPβ₁, β₂, D₁, H₂, glucagon
Gi↓ Adenylyl cyclase↓ cAMPα₂, M₂, D₂, opioid
Gq↑ PLCIP₃ + DAG + Ca²⁺α₁, M₁/M₃, 5‑HT₂
📌 High-Yield
  • Partial agonists act as antagonists when co-administered with full agonists
  • First-pass metabolism reduces oral bioavailability; IV = 100%
  • Time to steady state = 4–5 × t½ (90% at 3.3 t½)
💊 CYP450 Inducers & Inhibitors
  • Inducers: rifampin, carbamazepine, phenytoin, St. John's wort, barbiturates
  • Inhibitors: azole antifungals, macrolides, grapefruit, ritonavir, cimetidine
🧠 Clinical Pearl
  • Loading dose = (Vd × Cp) / f ; Maintenance dose = (Cl × Cpss × τ) / f
  • t½ = 0.7 × Vd / Cl

Autonomic Pharmacology

4 topics

🧪 Cholinergic Pharmacology

  • Synthesis: choline → ChAT → ACh → vesicle (via H⁺/ACh exchanger)
  • Release: Ca²⁺-dependent exocytosis; botulinum toxin blocks SNARE proteins
  • Termination: AChE hydrolyzes ACh → choline + acetate
ReceptorCouplingEffectorLocation
M₁, M₃, M₅Gq↑ PLC → IP₃/DAG/Ca²⁺Glands, smooth muscle
M₂, M₄Gi↓ AC → ↓ cAMPHeart, presynaptic
NNIon channelNa⁺/K⁺ fluxGanglia, adrenal medulla
NMIon channelNa⁺/K⁺ fluxNeuromuscular junction
AChE inhibitor ↑ synaptic ACh Muscarinic + Nicotinic effects
⚠️ Exam Trap
  • Physostigmine crosses BBB (tertiary amine); neostigmine does not (quaternary)
  • Organophosphate toxicity: atropine for muscarinic effects + pralidoxime (2‑PAM) for AChE reactivation
💊 Key Drugs
  • Direct agonists: pilocarpine (glaucoma), bethanechol (ileus/retention)
  • AChE inhibitors: neostigmine (myasthenia), donepezil (Alzheimer), physostigmine (antidote)
  • Antagonists: atropine (antidote, bradycardia), ipratropium (COPD), scopolamine (motion sickness)

⚡ Adrenergic Pharmacology

  • Synthesis: tyrosine → (tyrosine hydroxylase) → DOPA → (DOPA decarboxylase) → DA → (DA β‑hydroxylase) → NE
  • Termination: reuptake (primary), MAO (intraneuronal), COMT (synaptic)
ReceptorG-proteinEffectorKey Effects
α₁Gq↑ Ca²⁺Vasoconstriction, mydriasis, bladder sphincter
α₂Gi↓ cAMP↓ NE release (presynaptic), platelet aggregation
β₁Gs↑ cAMP↑ HR, contractility, conduction, renin
β₂Gs↑ cAMPBronchodilation, vasodilation, glycogenolysis
β₃Gs↑ cAMPDetrusor relaxation (overactive bladder)
🧠 Clinical Pearl
  • Epinephrine reversal: α-blockade unmasks β₂ vasodilation → BP drops
  • Norepinephrine: α₁ + β₁; no β₂ (so no vasodilation)
  • Dobutamine: β₁ > β₂ (inotrope in CHF)
💊 Beta Blockers
  • β₁-selective: metoprolol, atenolol, acebutolol (safer in asthma)
  • Non-selective: propranolol, timolol (glaucoma, migraine)
  • ISA: pindolol, acebutolol (less bradycardia)
  • α+β: carvedilol, labetalol (CHF, hypertensive emergencies)

🔄 ANS & Blood Pressure Control

  • BP = CO × TPR
  • Baroreceptor reflex: ↑ BP → ↑ PANS, ↓ SANS → ↓ HR, ↓ CO, ↓ TPR
  • Renin-angiotensin: ↓ renal perfusion → renin → Ang I → (ACE) → Ang II → vasoconstriction + aldosterone
↓ BP ↓ baroreceptor firing ↑ SANS / ↓ PANS ↑ HR, ↑ TPR, ↑ CO
⚠️ Exam Trap
  • Ganglionic blockers (mecamylamine) abolish reflex tachycardia
  • Muscarinic blockers (atropine) prevent reflex bradycardia
  • β₁ blockers prevent reflex tachycardia
🧠 Ocular Pharmacology
  • Atropine (M antagonist) → mydriasis + cycloplegia (near vision loss)
  • Phenylephrine (α₁ agonist) → mydriasis, no cycloplegia
  • Pilocarpine (M agonist) → miosis, ↑ aqueous outflow (glaucoma)
🫀

Cardiovascular Pharmacology

6 topics

💊 Antihypertensive Agents

ClassMechanismPrototypeKey Side Effect
Thiazide↓ Na⁺/Cl⁻ cotransporter (DCT)HydrochlorothiazideHypokalemia, hyperuricemia
ACEI↓ Ang II productionLisinoprilCough, angioedema, hyperkalemia
ARBAT₁ receptor blockadeLosartanNo cough (bradykinin spared)
CCB (DHP)Vascular Ca²⁺ blockadeNifedipineReflex tachycardia, gingival hyperplasia
CCB (non-DHP)Cardiac Ca²⁺ blockadeVerapamilConstipation, bradycardia
α₁-blockerVascular smooth muscle relaxationPrazosinOrthostatic hypotension
💊 Comorbidity-Guided Selection
  • Diabetes / CKD: ACEI or ARB (renoprotective)
  • Heart failure (↓EF): ACEI/ARB + beta-blocker
  • Post-MI: beta-blocker (mortality benefit)
  • BPH: alpha-blocker (dual benefit)
  • Pregnancy: methyldopa, labetalol (ACEI/ARB contraindicated)
🧠 Hypertensive Emergency
  • IV agents: nitroprusside (cyanide toxicity), labetalol, fenoldopam (D₁ agonist)
  • Nitroprusside toxicity: cyanide → metabolic acidosis; antidote = hydroxocobalamin + thiosulfate

💧 Diuretics

ClassSiteMechanismElectrolyte Effect
LoopTALNa⁺/K⁺/2Cl⁻ cotransporter↓ Na⁺, K⁺, Ca²⁺, Mg²⁺
ThiazideDCTNa⁺/Cl⁻ cotransporter↓ Na⁺, K⁺; ↑ Ca²⁺
K⁺-sparingCollecting ductNa⁺ channel / aldosterone antagonist↓ Na⁺; ↑ K⁺
CA inhibitorPCTCarbonic anhydrase inhibitor↓ Na⁺, HCO₃⁻; ↓ K⁺
OsmoticEntire nephronOsmotic retentionWater loss
⚠️ Exam Trap
  • Loop diuretics ↑ Ca²⁺ excretion; thiazides ↓ Ca²⁺ excretion
  • Sulfonamide cross-reactivity: CA inhibitors, loops (except ethacrynic acid), thiazides
  • Ethacrynic acid: no sulfa, greatest ototoxicity
  • K⁺-sparing + ACEI/ARB = hyperkalemia risk
💊 Key Uses
  • Loop: pulmonary edema, CHF, hypercalcemia
  • Thiazide: hypertension, nephrolithiasis (↓ Ca²⁺ stones)
  • Spironolactone: CHF, cirrhosis, hirsutism (anti-androgen)
  • Mannitol: cerebral edema, glaucoma, oliguric AKI

🫀 Antianginal Agents

ClassMechanismStable AnginaVasospastic Angina
Nitrates↓ preload, ↓ afterload, coronary vasodilation
Beta-blockers↓ HR, ↓ contractility
CCBs (DHP)↓ afterload, coronary vasodilation✅ (preferred)
Ranolazine↓ Na⁺/Ca²⁺ overload, ↓ demandLimited
⚠️ Exam Trap
  • Beta-blockers are contraindicated in vasospastic (Prinzmetal) angina — can worsen spasm
  • Nitrates + PDE5 inhibitors (sildenafil) = profound hypotension (contraindicated)
  • Nitrate tolerance: provide 8–12 hour nitrate-free interval
🧠 Clinical Pearl
  • Sublingual nitroglycerin: rapid onset (1–3 min), short duration (~30 min) — acute episode
  • Isosorbide mononitrate: longer duration, chronic maintenance

⚡ Antiarrhythmic Agents (Vaughan Williams)

ClassMechanismPrototypeECG Effect
IANa⁺ blockade + K⁺ blockadeQuinidine↑ QRS, ↑ QT
IBNa⁺ blockade (inactivated channels)Lidocaine↓ QT (mild)
ICNa⁺ blockade (potent)Flecainide↑ QRS
IIβ-blockadeMetoprolol↓ HR, ↑ PR
IIIK⁺ blockadeAmiodarone↑ QT, ↑ QRS
IVCa²⁺ blockadeVerapamil↓ HR, ↑ PR
💊 Key Agents
  • Amiodarone: multi-class (I, II, III, IV); pulmonary fibrosis, corneal deposits, thyroid dysfunction
  • Lidocaine: ventricular arrhythmias (post-MI); CNS toxicity (seizures)
  • Adenosine: PSVT; transient asystole; antagonized by methylxanthines
  • Dronedarone: similar to amiodarone, fewer thyroid/pulmonary effects; contraindicated in decompensated HF
⚠️ Exam Trap
  • Class IC drugs (flecainide) contraindicated in structural heart disease (CAST trial)
  • Class III drugs prolong QT → risk of torsades de pointes
  • Amiodarone has a half-life > 80 days (large Vd)

💊 Heart Failure Pharmacology

  • HFrEF (EF ≤ 40%): ACEI/ARB + β-blocker + aldosterone antagonist ± ARNI
  • HFpEF (EF ≥ 50%): β-blockers + diuretics (symptom control)
DrugMechanismMortality Benefit
ACEI/ARB↓ Ang II, ↓ afterload/preload
β-blockers (carvedilol, bisoprolol, metoprolol)↓ SNS activity, ↓ remodeling
Spironolactone / EplerenoneAldosterone receptor blockade
Sacubitril/valsartan (ARNI)Neprilysin inhibitor + ARB✅ (superior to ACEI)
DigoxinNa⁺/K⁺-ATPase inhibitor❌ (symptom benefit only)
💊 Inotropes (Acute CHF)
  • Dobutamine: β₁ agonist, ↑ contractility, mild vasodilation
  • Milrinone: PDE III inhibitor, ↑ cAMP, ↑ inotropy + ↓ TPR
  • Dopamine: dose-dependent (low: D₁, moderate: β₁, high: α)
⚠️ Digoxin Toxicity
  • Early: anorexia, nausea, vomiting
  • Late: confusion, visual disturbances (yellow-green halos), arrhythmias
  • Management: digoxin immune Fab (antidote), correct electrolytes
  • Interactions: diuretics (↓ K⁺), quinidine, verapamil (↑ digoxin levels)

📊 Lipid-Lowering Drugs

ClassPrimary EffectKey Adverse Effect
Statins↓↓ LDL (≥50%)Myopathy, hepatotoxicity
Bile Acid Sequestrants↓ LDL (modest)↑ TG, GI distress
Niacin↓ LDL, ↑↑ HDL, ↓ TGFlushing, hepatotoxicity
Fibrates↓↓ TG, ↑ HDLMyositis, gallstones
Ezetimibe↓ LDL (15–20%)GI distress
PCSK9 Inhibitors↓↓↓ LDL (50–60%)Injection site reactions
🧠 Clinical Pearl
  • Statins are first-line for LDL reduction; high-intensity: atorvastatin 40–80 mg, rosuvastatin 20–40 mg
  • Gemfibrozil + statin = ↑ myopathy risk (avoid)
  • PCSK9 inhibitors: alirocumab, evolocumab — dramatic LDL reduction
⚠️ Exam Trap
  • Niacin does NOT improve cardiovascular outcomes when added to statins
  • Bile acid sequestrants bind other oral drugs — separate dosing (1 h before / 4 h after)
🧠

CNS Pharmacology

6 topics

🧬 Dopamine Pathways & Drugs

PathwayFunctionDysfunction
NigrostriatalMotor controlParkinson (↓ DA), EPS (DA blockade)
MesolimbicReward, psychosisSchizophrenia (↑ DA → positive symptoms)
MesocorticalCognition, affectSchizophrenia (↓ DA → negative symptoms)
TuberoinfundibularProlactin inhibitionHyperprolactinemia (DA blockade)
💊 Parkinson Disease Drugs
  • Levodopa + carbidopa: gold standard; carbidopa is peripheral AAAD inhibitor
  • COMT inhibitors: entacapone, tolcapone (↑ levodopa bioavailability)
  • MAO-B inhibitors: selegiline, rasagiline (↓ DA metabolism)
  • DA agonists: pramipexole, ropinirole (D2/D3 stimulation)
  • Antimuscarinics: benztropine, trihexyphenidyl (tremor, rigidity)
⚠️ Exam Trap
  • Carbidopa does NOT cross BBB — only peripheral AAAD inhibition
  • Levodopa-induced dyskinesias correlate with disease duration and dose
  • Antipsychotic-induced EPS: treat with diphenhydramine or benztropine

💊 Antidepressants

ClassMechanismExamplesKey Side Effects
SSRISERT blockadeFluoxetine, sertralineSexual dysfunction, GI, serotonin syndrome
SNRISERT + NET blockadeVenlafaxine, duloxetineHypertension (venlafaxine), hepatotoxicity (duloxetine)
TCANon-selective reuptake blockadeAmitriptyline, imipramineAnticholinergic, cardiotoxicity, sedation
MAOIMAO inhibitionPhenelzine, tranylcypromineHypertensive crisis (tyramine), serotonin syndrome
BupropionDA + NE reuptake inhibitionBupropionInsomnia, seizures (lowers threshold)
Mirtazapineα₂ antagonist, H₁ antagonistMirtazapineWeight gain, sedation
⚠️ Serotonin Syndrome
  • Triad: altered mental status, autonomic instability, neuromuscular excitation
  • Trigger: SSRI + MAOI, SSRI + TCA, SSRI + meperidine
  • Management: discontinue agents, supportive care, cyproheptadine (antidote)
🧠 Clinical Pearl
  • SSRIs are first-line for depression and anxiety disorders
  • MAOIs require 2-week washout when switching to/from other antidepressants
  • Fluoxetine has the longest half-life → lowest withdrawal risk

💤 Sedative-Hypnotics & Anxiolytics

DrugGABAA EffectKey Features
Benzodiazepines↑ frequency of Cl⁻ channel openingCeiling effect, flumazenil antidote
Barbiturates↑ duration of Cl⁻ channel openingNo ceiling, CYP inducer, no antidote
Zolpidem / ZaleplonBZ₁ (α₁) selective agonistSleep onset, less cognitive impairment
Buspirone5-HT₁ₐ partial agonistNon-sedating, delayed onset (weeks)
⚠️ Exam Trap
  • Barbiturate withdrawal can be life-threatening (seizures, delirium tremens)
  • BZ withdrawal managed by gradual tapering; abrupt cessation → seizures
  • Flumazenil reverses BZ effects, NOT barbiturates or ethanol
  • Buspirone is NOT useful for acute anxiety or panic

⚡ Anticonvulsants

Seizure TypePreferred AgentsKey Notes
Focal (partial)Valproic acid, phenytoin, carbamazepine, lamotrigineLamotrigine better tolerated long-term
Generalized tonic-clonicValproic acid, phenytoin, carbamazepine, lamotrigineCarbamazepine may worsen absence/myoclonic
Absence (petit mal)Ethosuximide, valproic acidEthosuximide is highly selective
Status epilepticusIV lorazepam, IV diazepam, IV phenytoin/fosphenytoinFosphenytoin is water-soluble, faster infusion
💊 Key Drug Features
  • Phenytoin: zero-order kinetics; gingival hyperplasia, hirsutism, megaloblastic anemia
  • Carbamazepine: auto-induction; SIADH → hyponatremia; aplastic anemia
  • Valproic acid: broadest spectrum; hepatotoxicity, teratogenic (neural tube defects)
  • Ethosuximide: T-type Ca²⁺ blockade; absence seizures only
  • Lamotrigine: Stevens-Johnson risk (slow titration required)
⚠️ Exam Trap
  • Do NOT use carbamazepine or phenytoin for absence seizures
  • Phenytoin zero-order kinetics: small dose increments cause disproportionate toxicity
  • Valproate inhibits CYP450 → ↑ lamotrigine levels

💊 Opioid Pharmacology

ReceptorEffectsEndogenous Ligand
μ (mu)Analgesia, euphoria, respiratory depression, miosis, constipationβ-endorphin
κ (kappa)Spinal analgesia, dysphoria, diuresisDynorphin
δ (delta)Analgesia, antidepressant-like effectsEnkephalins
💊 Key Opioids
  • Morphine: prototype; metabolite M6G active; renal excretion
  • Fentanyl: high potency; lipophilic; transdermal, IV
  • Methadone: long-acting; NMDA antagonist; maintenance therapy
  • Buprenorphine: partial μ agonist; ceiling effect; lower respiratory depression
  • Meperidine: anticholinergic; normeperidine → seizures; avoid in renal impairment
🧠 Clinical Pearl
  • Opioid toxicity triad: miosis + respiratory depression + coma
  • Naloxone is the antidote; duration shorter than most opioids → monitor for re-sedation
  • Constipation and miosis do NOT develop tolerance
  • Loperamide is a peripheral μ agonist (does not cross BBB) — antidiarrheal
⚠️ Exam Trap
  • Meperidine is the exception to miosis (causes mydriasis)
  • Mixed agonist-antagonists (pentazocine, nalbuphine) can precipitate withdrawal in opioid-dependent patients

💉 Anesthesia & Muscle Relaxants

AgentMAC (%)Blood-Gas RatioKey Feature
Nitrous oxide1040.5Very rapid onset/recovery; weak
Sevoflurane20.6Sweet odor; preferred for mask induction
Desflurane60.5Very low solubility; pungent; heated vaporizer
💊 IV Anesthetics
  • Propofol: rapid onset, antiemetic, negative inotrope; pain on injection
  • Ketamine: NMDA antagonist; sympathomimetic; preserves airway reflexes; emergence delirium
  • Midazolam: BZ; anterograde amnesia; respiratory depression
  • Fentanyl: synthetic opioid; chest wall rigidity (rapid bolus)
🧠 Neuromuscular Blockers
  • Succinylcholine: depolarizing; rapid onset (30–60 s); short duration; hyperkalemia risk; MH trigger
  • Rocuronium: non-depolarizing; competitive antagonist; reversed by neostigmine
  • Malignant hyperthermia: dantrolene is the antidote; trigger: succinylcholine + volatile anesthetics
⚠️ Exam Trap
  • Low MAC = high potency (not fast onset)
  • Succinylcholine contraindicated in burns, trauma, denervation (hyperkalemia)
  • Dantrolene inhibits RyR1 (skeletal muscle Ca²⁺ release)
🦠

Antimicrobial Pharmacology

4 topics

🧫 Antibacterial Agents

ClassMechanismExamplesKey Adverse Effect
PenicillinsCell wall (PBPs)Amoxicillin, piperacillin, nafcillinHypersensitivity, GI
CephalosporinsCell wall (PBPs)Ceftriaxone, cefepimeHypersensitivity (5% cross-reactivity)
CarbapenemsCell wall (PBPs)Imipenem, meropenemSeizures (imipenem)
VancomycinCell wall (D-Ala-D-Ala)VancomycinRed man syndrome, nephrotoxicity, ototoxicity
Aminoglycosides30S ribosomeGentamicin, tobramycinNephrotoxicity, ototoxicity
Macrolides50S ribosomeAzithromycin, clarithromycinQT prolongation, GI
Tetracyclines30S ribosomeDoxycycline, minocyclinePhototoxicity, tooth discoloration
FluoroquinolonesDNA gyraseCiprofloxacin, levofloxacinTendon rupture, cartilage damage
MetronidazoleDNA damageMetronidazoleDisulfiram-like with alcohol
💊 Drug of Choice
  • MRSA: vancomycin, linezolid, daptomycin
  • Pseudomonas: antipseudomonal penicillins, ceftazidime, cefepime, carbapenems, aminoglycosides
  • UTI: TMP-SMX, nitrofurantoin, fluoroquinolones
  • STIs: ceftriaxone (gonorrhea), doxycycline/azithromycin (chlamydia), penicillin G (syphilis)
⚠️ Exam Trap
  • Bactericidal + bacteriostatic combinations can be antagonistic (e.g., tetracycline + penicillin)
  • TMP-SMX is DOC for Pneumocystis jirovecii and Nocardia
  • Metronidazole is DOC for C. difficile colitis

🫁 Antitubercular Drugs

DrugMechanismKey Adverse Effect
Isoniazid (INH)Mycolic acid synthesisHepatitis, peripheral neuritis (B6), SLE (slow acetylators)
RifampinRNA polymerase inhibitionHepatitis, P450 induction, orange-red secretions
EthambutolArabinogalactan synthesisRetrobulbar neuritis (red-green color vision)
PyrazinamideUnknown (acidic environment)Hepatitis, hyperuricemia (gout)
Streptomycin30S ribosome (aminoglycoside)Ototoxicity, nephrotoxicity
🧠 Clinical Pearl
  • Standard 4-drug regimen: INH + rifampin + ethambutol + pyrazinamide
  • Always give pyridoxine (B6) with INH to prevent peripheral neuropathy
  • Rifampin induces P450 → reduces efficacy of OCPs, warfarin, etc.

🧫 Antifungal Drugs

ClassMechanismExamplesKey Adverse Effect
PolyenesErgosterol binding (pores)Amphotericin B, nystatinNephrotoxicity, infusion reactions
Azoles14α-demethylase inhibitionFluconazole, voriconazoleHepatotoxicity, CYP inhibition
Echinocandinsβ-glucan synthase inhibitionCaspofungin, micafunginInfusion reactions, hepatotoxicity
FlucytosineDNA/RNA synthesis inhibitionFlucytosineBone marrow suppression
TerbinafineSqualene epoxidase inhibitionTerbinafineHepatotoxicity, dysgeusia
💊 Key Uses
  • Cryptococcal meningitis: Amphotericin B + flucytosine (induction), fluconazole (consolidation)
  • Invasive aspergillosis: voriconazole (DOC)
  • Mucormycosis: amphotericin B
  • Onychomycosis: terbinafine (first-line)
⚠️ Exam Trap
  • Fluconazole has excellent CNS penetration; does NOT cover Aspergillus
  • Liposomal amphotericin B has less nephrotoxicity than conventional
  • Azoles inhibit CYP450 → multiple drug interactions

🧬 Antiviral Agents

VirusDrugMechanismKey Adverse Effect
HSV/VZVAcyclovirDNA polymerase (chain terminator)Nephrotoxicity (IV), neurotoxicity
CMVGanciclovirDNA polymeraseHematotoxicity, nephrotoxicity
HIVNRTIs (zidovudine)Reverse transcriptaseHematotoxicity, neuropathy
HIVNNRTIs (efavirenz)Reverse transcriptaseCNS effects, rash
HIVPIs (ritonavir)Protease inhibitionMetabolic syndrome, CYP inhibition
InfluenzaOseltamivir, zanamivirNeuraminidase inhibitionGI, bronchospasm (zanamivir)
HCVSofosbuvirNS5B polymerase inhibitionFatigue, headache
🧠 Clinical Pearl
  • Acyclovir resistance: most commonly due to TK deficiency
  • Foscarnet: direct DNA polymerase inhibitor; nephrotoxic; used for acyclovir-resistant HSV
  • HAART: combination of 3–4 drugs; never use monotherapy
  • Ritonavir: used as PK booster (CYP3A4 inhibition)
⚠️ Exam Trap
  • Amantadine/rimantadine no longer recommended for influenza due to resistance
  • NNRTIs have a low genetic barrier — single mutation confers resistance
  • Protease inhibitors are associated with metabolic syndrome (insulin resistance, dyslipidemia)
🧬

Autacoids & Inflammation

3 topics

🧪 Histamine & Antihistamines

ReceptorCouplingEffectsAntagonist
H₁GqVasodilation, bronchoconstriction, itchDiphenhydramine, loratadine
H₂GsGastric acid secretion, ↑ HRCimetidine, famotidine
H₃GiPresynaptic inhibition
💊 Key Agents
  • First-generation (sedating): diphenhydramine, promethazine, meclizine — cross BBB, anticholinergic
  • Second-generation (non-sedating): loratadine, fexofenadine, cetirizine — limited CNS penetration
  • H₂ antagonists: cimetidine (CYP inhibitor, anti-androgenic), famotidine (preferred)
⚠️ Exam Trap
  • Cimetidine inhibits CYP450 → drug interactions; famotidine does not
  • Cetirizine can cause mild sedation (unlike loratadine/fexofenadine)
  • First-generation antihistamines contraindicated in elderly (anticholinergic → dementia risk)

🧠 Serotonin, Migraine & NSAIDs

DrugReceptor TargetUse
Sumatriptan (triptan)5-HT₁B/DAcute migraine (vasoconstriction)
Ergotamine5-HT₂, αAcute migraine (second-line)
Ondansetron5-HT₃Chemotherapy-induced nausea
Cyproheptadine5-HT₂, H₁Serotonin syndrome, carcinoid
Buspirone5-HT₁ₐGAD (delayed onset)
💊 NSAIDs & COX Inhibitors
  • Non-selective COX inhibitors: aspirin, ibuprofen, naproxen — GI ulcers, bleeding
  • COX-2 selective: celecoxib — less GI toxicity, ↑ CV risk
  • Acetaminophen: central COX inhibition; safe for GI/bleeding risk; hepatotoxicity in overdose (N-acetylcysteine antidote)
  • Aspirin: irreversible COX-1 inhibition; antiplatelet for 7–10 days; Reye syndrome in children
⚠️ Exam Trap
  • Triptans contraindicated in CAD and uncontrolled hypertension
  • Ergotamine is NOT first-line; contraindicated in pregnancy, CAD, and hypertension
  • COX-2 inhibitors increase cardiovascular risk (unopposed TXA₂)

🦴 Rheumatic & Inflammatory Disorders

DrugMechanismUseKey Side Effect
MethotrexateFolate antagonistRA (first-line DMARD)Hepatotoxicity, myelosuppression
HydroxychloroquineLysosomal stabilizationRA, SLERetinopathy (annual eye exam)
SulfasalazineB-cell inhibitionRA, IBDHemolysis (G6PD)
LeflunomideDHODH inhibitionRAHepatotoxicity, teratogenic
TNF inhibitorsTNF-α blockadeRA, IBD, psoriasisInfections (TB screening)
JAK inhibitorsJAK-STAT inhibitionRAInfections, thrombosis
🧠 Gout Therapy
  • Acute: NSAIDs, colchicine (microtubule inhibition), glucocorticoids
  • Chronic: allopurinol (xanthine oxidase inhibitor), febuxostat, probenecid (uricosuric)
  • Refractory: pegloticase (urate oxidase)
  • Colchicine: narrow therapeutic index; diarrhea is dose-limiting; CYP3A4 interaction
⚠️ Exam Trap
  • Do NOT start urate-lowering therapy during an acute gout flare
  • Allopurinol dose adjustment in renal impairment
  • Probenecid requires GFR > 50 mL/min
🩸

Hematologic Pharmacology

1 topic

💉 Anticoagulants, Thrombolytics & Antiplatelets

DrugMechanismMonitoringReversal
HeparinATIII-mediated IIa/Xa inhibitionaPTTProtamine sulfate
LMWH (enoxaparin)ATIII-mediated Xa inhibitionAnti-Xa (usually not needed)Protamine (partial)
WarfarinVitamin K antagonist (II, VII, IX, X)PT/INRVitamin K, FFP
DabigatranDirect thrombin inhibitorNone (routine)Idarucizumab
Rivaroxaban, apixabanDirect Xa inhibitorNone (routine)Andexanet alfa
AspirinIrreversible COX-1 inhibitionNonePlatelet transfusion
ClopidogrelP2Y₁₂ (ADP receptor) inhibitionNonePlatelet transfusion
tPA (alteplase)Fibrin-bound plasminogen activationNoneAminocaproic acid, tranexamic acid
🧠 Clinical Pearl
  • Factor VII has the shortest half-life (~6 h) → warfarin affects PT/INR first
  • Protein C half-life ~8 h → warfarin can cause transient hypercoagulability (skin necrosis)
  • HIT: platelet drop >50% on days 5–10; stop heparin, use argatroban
  • Dual antiplatelet therapy (ASA + P2Y₁₂ inhibitor) after drug-eluting stent
⚠️ Exam Trap
  • Heparin does NOT cross the placenta (safe in pregnancy); warfarin is teratogenic
  • LMWH has less HIT and osteoporosis risk than unfractionated heparin
  • tPA for stroke: time window 3–4.5 hours; rule out hemorrhage first
🧪

Endocrine & Metabolic Pharmacology

2 topics

🩸 Diabetes & Metabolic Drugs

ClassMechanismExamplesKey Side Effect
Biguanides↑ insulin sensitivity, ↓ gluconeogenesisMetforminGI, lactic acidosis (renal impairment)
Sulfonylureas↑ insulin release (K⁺ channel blockade)Glipizide, glyburideHypoglycemia, weight gain
ThiazolidinedionesPPARγ agonistsPioglitazone, rosiglitazoneWeight gain, edema, CV risk (rosiglitazone)
GLP-1 agonistsGLP-1 receptor activationLiraglutide, semaglutideNausea, vomiting, pancreatitis
DPP-4 inhibitors↑ endogenous GLP-1SitagliptinWeight neutral, low hypoglycemia risk
SGLT-2 inhibitors↓ glucose reabsorption (kidney)Canagliflozin, empagliflozinUTI, genital mycotic, osmotic diuresis
α-glucosidase inhibitors↓ carbohydrate digestionAcarboseFlatulence, diarrhea
💊 Insulin Preparations
  • Rapid-acting (lispro): onset 0.3–0.5 h, peak 1–2 h, duration 3–4 h
  • Short-acting (regular): onset 0.5–1 h, peak 2–4 h, duration 5–7 h
  • Long-acting (glargine): onset 1 h, no pronounced peak, duration ≥24 h
  • Regular insulin is the only IV insulin (DKA, perioperative)
🧠 Clinical Pearl
  • Metformin is first-line for Type 2 diabetes (weight neutral, no hypoglycemia)
  • SGLT-2 inhibitors have cardiorenal protective effects
  • Hypoglycemia management: oral glucose (conscious), IV dextrose (unconscious), glucagon (if no IV)

🦋 Thyroid & Adrenal Pharmacology

DrugMechanismUseKey Side Effect
PTU (propylthiouracil)Thyroid peroxidase inhibition + T₄→T₃ inhibitionHyperthyroidism (pregnancy preferred)Hepatotoxicity, agranulocytosis
MethimazoleThyroid peroxidase inhibitionHyperthyroidismAgranulocytosis, aplasia cutis (pregnancy)
Radioactive iodine (¹³¹I)Selective thyroid destructionGraves disease, toxic nodulesHypothyroidism (common)
Levothyroxine (T₄)Thyroid hormone replacementHypothyroidismHyperthyroidism (overdose)
DexamethasoneGlucocorticoid (long-acting)Inflammation, cerebral edema, COVID-19HPA suppression, osteoporosis
PrednisoneGlucocorticoid (intermediate)Inflammatory disordersHPA suppression, weight gain
FludrocortisoneMineralocorticoidAdrenal insufficiency (salt-wasting)Hypertension, edema
⚠️ Exam Trap
  • PTU preferred in pregnancy (less placental transfer than methimazole)
  • Thyroid storm: PTU + iodide + propranolol + glucocorticoids
  • Glucocorticoid withdrawal: taper slowly to avoid adrenal crisis
  • Dexamethasone has negligible mineralocorticoid activity
🫁

Respiratory & GI Pharmacology

1 topic

🫁 Asthma/COPD & GI Therapeutics

ClassMechanismExamplesKey Feature
SABAβ₂ agonist (short-acting)AlbuterolAcute bronchospasm (5–15 min onset)
LABAβ₂ agonist (long-acting)Salmeterol, formoterolNever as monotherapy (↑ asthma death)
ICSGlucocorticoid (inhaled)Budesonide, fluticasoneFirst-line controller; thrush (rinse mouth)
Muscarinic antagonistM₃ blockadeIpratropium, tiotropiumCOPD first-line; no CNS effects
AntileukotrienesLTD₄ receptor antagonistMontelukastExercise-induced asthma; neuropsychiatric effects
PDE-4 inhibitorPDE-4 inhibitionRoflumilastSevere COPD with exacerbations
PPIH⁺/K⁺-ATPase inhibitionOmeprazoleGERD, ulcer; irreversible; B₁₂ deficiency with long-term
H₂ antagonistH₂ receptor blockadeFamotidineGERD, ulcer (less potent than PPI)
MisoprostolPGE₁ analogMisoprostolNSAID ulcer prophylaxis; abortifacient (contraindicated in pregnancy)
🧠 Clinical Pearl
  • Asthma: SABA for acute relief; ICS for chronic control
  • COPD: tiotropium (LAMA) is first-line maintenance
  • Montelukast: FDA boxed warning for neuropsychiatric effects
  • PPIs are the most potent acid suppressants; long-term use → B₁₂ deficiency, osteoporosis, C. difficile
⚠️ Exam Trap
  • LABA monotherapy increases asthma-related death — always use with ICS
  • Misoprostol is a teratogen — contraindicated in pregnancy
  • Metronidazole + alcohol = disulfiram-like reaction
🌀

Neuropharmacology: Drugs of Abuse

1 topic

🧠 Drugs of Abuse & Withdrawal

Drug ClassMechanismKey FeaturesWithdrawal
Stimulants (cocaine, amphetamines)↑ DA, NE, 5HT (reuptake/release)Euphoria, tachycardia, hypertension, psychosisDepression, anhedonia (not life-threatening)
Depressants (BZ, barbiturates, ethanol)GABAA potentiationSedation, respiratory depression (barbiturates > BZ)Seizures, delirium tremens (ethanol, barbiturates) — life-threatening
Opioidsμ receptor agonismEuphoria, miosis, respiratory depressionLacrimation, piloerection, diarrhea (not life-threatening)
Hallucinogens (LSD, psilocybin)5-HT₂ₐ agonismPerceptual distortions, sympatheticsNo classic dependence
Marijuana (THC)CB₁ receptor agonismSedation, euphoria, tachycardia, red eyesMild (irritability, insomnia)
PCP / KetamineNMDA receptor antagonismDissociation, nystagmus (PCP)Not well-characterized
💊 Clinical Management
  • Opioid overdose: naloxone (repeated doses)
  • BZ overdose: flumazenil (caution in chronic users → seizures)
  • Barbiturate/ethanol withdrawal: benzodiazepines (diazepam)
  • Stimulant toxicity: benzodiazepines, cooling measures
⚠️ Exam Trap
  • Miosis is characteristic of opioids; meperidine causes mydriasis
  • PCP intoxication: nystagmus (horizontal + vertical)
  • MDMA toxicity: hyperthermia + hyponatremia
🎯

Oncology & Toxicology

2 topics

🎯 Anticancer, Immune & Toxicology

DrugMechanismKey ToxicityAntidote / Protection
CyclophosphamideAlkylating agentHemorrhagic cystitisMesna (acrolein trap)
CisplatinDNA cross-linksNephrotoxicity, ototoxicityAmifostine, hydration
DoxorubicinIntercalation, free radicalsCardiomyopathy (delayed)Dexrazoxane (iron chelator)
MethotrexateDHFR inhibitorMyelosuppressionLeucovorin (rescue)
BleomycinDNA strand scissionPulmonary fibrosis
VincristineMicrotubule inhibitionNeurotoxicity
ATRADifferentiationDifferentiation syndromeCorticosteroids
💊 Immunosuppressants
  • Cyclosporine / Tacrolimus: calcineurin inhibitors; nephrotoxicity; gingival hyperplasia (cyclosporine)
  • Mycophenolate: purine synthesis inhibitor (lymphocyte-selective)
  • Azathioprine: prodrug → 6-mercaptopurine; myelosuppression
  • Anti-TNF: infliximab, adalimumab; TB screening required
🧠 Clinical Pearl
  • Log-kill hypothesis: cytotoxic drugs kill a constant fraction of cells
  • Cell-cycle specific (CCS): methotrexate, 5-FU, vincristine
  • Cell-cycle non-specific: alkylating agents, cisplatin, doxorubicin

🧪 Toxic Alcohols & Poisoning

AlcoholToxic MetaboliteEnd-Organ DamageTreatment
MethanolFormic acidOptic neuropathy, blindness, metabolic acidosisFomepizole, ethanol, folate, hemodialysis
Ethylene glycolGlycolic acid → oxalic acidRenal failure, calcium oxalate crystals, hypocalcemiaFomepizole, ethanol, thiamine, pyridoxine, hemodialysis
EthanolAcetaldehyde → acetateCNS depression, hypoglycemia (children)Supportive care, thiamine, glucose
💊 Antidotes
  • Fomepizole (4-methylpyrazole): competitive ADH inhibitor; drug of choice for methanol/ethylene glycol
  • Ethanol: alternative ADH substrate (second-line)
  • Hemodialysis: indicated for severe acidosis (pH < 7.2), end-organ damage, or high levels (>50 mg/dL)
⚠️ Exam Trap
  • Methanol → visual symptoms + anion-gap acidosis + osmolar gap
  • Ethylene glycol → renal failure + calcium oxalate crystals + hypocalcemia
  • Ethanol → osmolar gap alone (no significant acidosis)
  • Disulfiram-like reaction: metronidazole + alcohol → ALDH inhibition → acetaldehyde buildup